The clinical hold is due to questions about BX004’s nebulizer device, temporarily pausing US enrollment in the cystic ...

The regulatory body determined that PTC Therapeutics’ New Drug Application for vatiquinone did not provide sufficient ...

The company plans to continue with a lower dose and a change in the pre-treatment regimen after a trial participant died ...

Rocket’s relatively quick reprieve is good news for the stock, and suggests that the FDA remains actively supportive of gene ...

The FDA recommends that companies use overall survival as a primary endpoint for clinical trials where feasible. The new ...

Dining under palm trees on a patio at Mar-a-Lago in December, President-elect Donald Trump reassured chief executives at ...

Far-right activist Laura Loomer is flexing her influence with the White House as she racks up policy and personnel wins from ...

Capricor Therapeutics met with the FDA last week for a type A meeting, during which CEO Linda Marbán aimed to explain to the ...

AAP published the new advice on Tuesday, saying it strongly recommends Covid shots for children ages 6 months to 2 years.

He’s using Biden-era mistakes to tarnish a promising technology.

A staffer for HHS Secretary Robert F Kennedy Jr - who drew the ire of President Donald Trump's MAGA base and was fired - ...