Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial.

The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...

The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...

A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...

A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

Caregiving means that columnist Betty Vertin sometimes misses out on activities with her children who don't have DMD. Finding balance is key.

Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.

For the second time, a person with DMD has died of acute liver failure after being treated with the one-time gene therapy Elevidys.

As a person living with DMD, these discussions struck a chord with me, because these types of issues profoundly affect my daily life.Healthcare interactions with patients with Duchenne often involve ...

I’m between two anniversaries. Today is the 36th anniversary of the collision I had with a drunk driver that cost me my eyesight and almost cost me my life. Saturday will be my 45th wedding ...