A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

A new article argues dystrophin immunogenicity is an under-examined issue in the treatment of Duchenne muscular dystrophy.

A few weeks after Sarepta Therapeutics confirmed a patient died after receiving its drug Elevidys, research published April 3 ...

Catalyst Pharmaceuticals (CPRX) reported that its sub-licensee in Canada, Kye Pharmaceuticals, has announced that Health Canada has accepted ...

Explore Solid Biosciences’ potential with promising SGT-003 trial results for DMD, strong financials, and market recovery ...

Biophytis SA (FP: ALBPS), ("Biophytis" or the "Company"), a clinical-stage biotechnology company specializing in the development of treatments for age-related diseases, confirms the launch of the ...

A surge of generics, biosimilars, and innovative therapies is expected in 2025, addressing conditions from cancer to chronic ...

Actor Matthew McConaughey, ex UT coach Mack Brown and country artist Jack Ingram have hosted the Mack, Jack & McConaughey ...

Today's pharmaceutical stocks are facing the challenges of government-imposed drug price caps, waning demand for COVID-19 ...

We recently published a list of 20 Stocks Insiders Bought in April After Trump’s Tariff Rollout. In this article, we are ...

ITV News has uncovered further allegations of neglect of disabled adults at Lifeways and at least one council has placed the company into special measures. | ITV National News ...

The determination comes after recruitment and dosing in certain trials were paused after a young patient died due to acute ...