Mother with rare ALS touts 'miracle drug' that has stopped her disease
Raziel Green, 52, an active runner and mother of two, was diagnosed with a rare form of ALS in 2017. Since starting a ...
New York Post13d
Mother with rare ALS touts ‘miracle drug’ that has stopped her disease
It wasn’t until she saw a third neurologist, who specialized in genetic diseases, that she was diagnosed with the superoxide dismutase 1 (SOD1) gene and amyotrophic lateral sclerosis (ALS).
Regina woman is living proof of 'breakthrough' ALS drug now approved in Canada
A Regina mother who was one of the first ALS patients to test a new treatment is now celebrating its accelerated approval in Canada for adults with an ultra-rare form of the disease.Paula Trefiak's ...
CBC.ca20d
Regina woman is living proof of 'breakthrough' ALS drug now approved in Canada
Health Canada confirms it has granted conditional approval to Qalsody to treat adults with ALS in cases linked to a mutation in the superoxide dismutase 1 (SOD1) gene. Paula Trefiak's grandmother ...
Metro22d
My husband’s muscles started twitching – he’s been given 3 years
The biggest source of hope for MND patients is that cases caused by a faulty SOD1 gene could be treated. However, this is very rare; just 2% of people have this type of MND. On the day Andrew ...
ALS News Today10d
MDA 2025: INS1202 gene therapy shows promise in SOD1-ALS mice
Preclinical data with the investigational gene therapy INS1202 show improvements in survival and motor performance in ALS.
pharmaphorum7d
Biogen gets FDA approval for ALS drug Qalsody
associated with a mutation in the SOD1 gene. The drug – branded as Qalsody – is the first therapy to be approved for a genetic form of ALS, and is also notable for being the first neurology ...