LUXTURNA has significant market potential due to the high unmet need for effective treatments in rare genetic conditions. With its FDA approval for specific mutations in the RPE65 gene, it offers ...
Explore daily insights on the USA TODAY crossword puzzle by Sally Hoelscher. Uncover expert takes and answers in our ...
A team of researchers from the Institute for Neurosciences, a joint center of the Spanish National Research Council (CSIC) and the Miguel Hernández University (UMH) of Elche, in collaboration with ...
AZoLifeSciences on MSN6d
Scientists Identify Crucial Mechanism for Maintaining Neuronal Identity in the BrainA team of researchers from the Institute for Neurosciences, a joint center of the Spanish National Research Council (CSIC) ...
Use of DYNE-101 is leading to improvements in muscle, and specifically finger, function in myotonic dystrophy type 1 patients ...
Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...
The discovery could pave the way for a groundbreaking RNA-based multi-cancer treatment. Alternative RNA splicing functions ...
Humans began changing plants as soon as they domesticated and cultivated them instead of just gathering them. Humans began ...
Transgenic worm in which the splicing factor UNC-75, marked with the fluorophore mScarlet, reveals its expression throughout the nervous system. The worm was generated using CRISPR-Cas9 gene editing ...
A team of researchers from the Institute for Neurosciences, a joint center of the Spanish National Research Council (CSIC) and the Miguel Hernández ...
The results of this work reveal how an alternative splicing mechanism regulates an essential factor for neuronal identity.
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