Cells have a natural editing system that allows them to rearrange genetic instructions to create different proteins from the ...

Alternative RNA splicing is like a movie editor cutting and rearranging scenes from the same footage to create different ...

BARCELONA, Spain I March 13, 2025 I SpliceBio, a clinical-stage genetic medicines company pioneering Protein Splicing to address diseases caused by mutations ...

Dyne Therapeutics’ DYNE-101 shows positive results in phase 1/2 ACHIEVE study. Read why DYN stock may rise with FDA approval and a $2.78B market opportunity.

Researchers at Kumamoto University have successfully executed a practical trial of a new genome-editing technique that allows ...

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

A human-specific NOVA1 variant changed mouse vocalizations, potentially providing insights into the evolution of language.

A new multi-omics approach to unpicking how noncoding gene variants influence the development of common chronic diseases has ...

Spliceosome structures have been investigated extensively in the past decade, but most of the studies have been restricted to ...

RNA sequencing has emerged as a powerful supplement to DNA sequencing for Mendelian disease diagnosis, but clinical ...

RNA sequencing has emerged as a powerful supplement to DNA sequencing for Mendelian disease diagnosis, but clinical ...