The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...

A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...

The FDA has informed Capricor Therapeutics the meeting should happen July 30, though Capricor said that date hasn’t been confirmed. At an advisory committee meeting, the FDA gathers independent ...

Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.