7-year-old in Hamilton has rare condition with $300K annual treatment her family can't afford
Cena Hermus, 7, was two years old when she was diagnosed with a rare, life-threatening disorder that causes severe obesity.
Mothers rally and urge action over access to drug
The mother of a six-year-old girl with a rare neurodegenerative disease has urged health bosses to "do the right thing" amid ...
Batten Disease: Parents fight for costly drug for children's rare disease to remain on NHS
Oliver and Amelia Carroll have Batten Disease - an incurable genetic disorder that causes rapid decline in a child's ability to walk, talk and see. | ITV News Granada ...
Director Who Worked With Prince Frederik Says it Was ‘Painful’ to Watch Him Struggle Before His Death
Filmmaker Mei Fa Tan reflected on her experience working with Luxembourg’s Prince Frederik before his death at the age of 22.
Terrifying and painful new skin disease ravages young father, with doctors warning it will kill him
A 39-year-old father is suffering from a horrifically painful skin disease that doctors can't cure or even definitively ...
Ex-doctor's 30-month term for assisted death of ALS patient upheld
The Osaka High Court on Thursday upheld a lower court ruling that sentenced a former doctor to two years and six months in ...
Preclinical study demonstrates improved gene therapy approach to treating a rare and devastating disease in children
In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with ...
Fierce Biotech22h
Ono pays $280M upfront for Ionis' antisense oligonucleotide for rare blood cancer
Japan's Ono Pharmaceutical is handing over $280 million upfront to acquire Ionis Pharmaceuticals’ phase 2-stage antisense ...
Fierce Biotech12h
Clario acquires WCG's neuroscience-focused clinical outcome assessment business
Tech firm Clario is boosting its electronic clinical outcome assessment (eCOA) offerings by acquiring the ...
The Times-Tribune17h
Eastern equine encephalitis virus killed horse in county, no human cases reported
A mosquito-borne viral disease exceedingly rare in people killed a horse in Lackawanna County, though no human cases have ...
Knowridge Science Report9h
Study finds new hope for Alzheimer’s disease prevention
A new international study has identified key genetic factors that may protect against Alzheimer’s disease (AD), offering ...
Bruce Willis' wife tributes Gene Hackman and Betsy Arakawa while calling for caregiver support
Bruce Willis ' wife, Emma Heming Willis, is sharing her thoughts following the deaths of Gene Hackman and his wife, Betsy ...