Setback in gene therapy for Duchenne muscular dystrophy as immune system emerges as key barrier
A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...
Mirage News11h
Gene Therapy for Duchenne Faces Immune System Hurdle
New research identifies the body's own immune response as a critical and previously underappreciated barrier to successEarly intervention at birth ...
Muscular Dystrophy News4h
Independent committee favors continuing Elevidys dosing in trials
The determination comes after recruitment and dosing in certain trials were paused after a young patient died due to acute ...