Scots children with muscular dystrophy denied free new life-extending drug
Patients in Scotland can't get the treatment - which is available in England - despite manufacturers giving it away for free ...
Managed Healthcare Executive2d
Caregiver Burden and Value Assessments in Duchenne Muscular Dystrophy
Doing more to incorporate caregiver burden into value assessments and cost-effectiveness research of Duchene muscular dystrophy treatments was the focus of a recent International Society for ...
ET HealthWorld3d
Parents of muscular dystrophic patients protest in Delhi, demand access to high-cost treatment
One of the demands raised during the protests was access to 'Elevidys', a one-time gene therapy treatment that has the ...
Managed Healthcare Executive3d
New Study Shows Duchenne's Effect on the Brain Might Be Reversed
Managed Healthcare Executive gives C-suite executives in health plans and provider organizations news and strategies for ...
BioSpace2d
Sarepta’s Duchenne Gene Therapy Placed on Hold in Europe Pending Death Investigation
The European Medicines Agency asked for three clinical trials to be placed on hold until the exact cause of death of a US ...
The Manila Times5d
Muscular Dystrophy Association and Burn Boot Camp Team Up for the 9th Annual 'Be Their Muscle' Philanthropic Event
Muscular Dystrophy Association and Burn Boot Camp Team Up for the 9th Annual 'Be Their Muscle' Philanthropic Event ...
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Sarepta/Roche Suspend Elevidys Gene Therapy Trials In Europe After Patient Death
Sarepta Therapeutics, Inc. (NASDAQ:SRPT) shared an update on Elevidys (delandistrogene moxeparvovec-rokl), the only approved ...
A mother’s battle: Advocating for life-saving treatments for children with Duchenne muscular dystrophy
When her son reached three last year, a new name loomed over their lives — Duchenne Muscular Dystrophy (DMD), a ...
Oxford Mail on MSN1h
Family hopes to take boys with life-limiting condition to Disneyland Paris
The family of two boys who both have a life-limiting condition are hoping to take a trip to Disneyland Paris later this year.
Defeat Duchenne Canada Launches 2025 Research Grant Cycle, Set to Commit its $20 Millionth Dollar to Groundbreaking Research
Defeat Duchenne Canada, the country's leading funder of Duchenne muscular dystrophy (DMD) research, is set to begin accepting innovative research proposals as of March 31, 2025. They are seeking ...