The Emerton family didn't know the odds were always stacked against them, all because of a rare gene. Already, that gene has sent both Clay Emerton and his son, Andrew, into cardiac arrest ...

imageimageDisrupting the expression of the minor spliceosome component RNPC3 reduces the growth of oncogene-driven cancer cells in a broad spectrum of tumours. Targeting the minor spliceosome may ...

Spain's SpliceBio has raised $135m in financing that will help it move a gene-editing therapy for Stargardt disease through clinical testing.