Preclinical data with the investigational gene therapy INS1202 show improvements in survival and motor performance in ALS.

Raziel Green, 52, an active runner and mother of two, was diagnosed with a rare form of ALS in 2017. Since starting a ...

From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing. Whether it's investigating the financials of Elon Musk's pro-Trump PAC or ...

Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders. Now it’s on the cusp of its first regulatory approval. Each year ...

Gene Hackman had only been spotted on a few rare appearances throughout the remainder of his life. The Royal Tenenbaums star hung up his hat on his iconic film career at the age of 74, and he died ...

Tau silencing gene therapy VY1706 robustly reduced tau mRNA levels, with broad distribution, and was well-tolerated in NHP study; IND filing ...

Health Canada confirms it has granted conditional approval to Qalsody to treat adults with ALS in cases linked to a mutation in the superoxide dismutase 1 (SOD1) gene. Paula Trefiak's grandmother ...

A Regina mother who was one of the first ALS patients to test a new treatment is now celebrating its accelerated approval in Canada for adults with an ultra-rare form of the disease.Paula Trefiak's ...

By Gina Kolata Researchers have corrected a disease-causing gene mutation with a single infusion carrying a treatment that precisely targeted the errant gene. This was the first time a mutated ...

New Mexico officials have announced the cause of death for actor Gene Hackman and his wife Betsy Arakawa, a week after they were found dead at their home in Santa Fe. Hackman died of heart disease ...

Ms. Arakawa, the wife of the actor Gene Hackman, died from the effects of a disease often caused by contact with droppings from infected rodents. By Hank Sanders and Michael Levenson Betsy Arakawa ...