Preclinical data with the investigational gene therapy INS1202 show improvements in survival and motor performance in ALS.
It wasn’t until she saw a third neurologist, who specialized in genetic diseases, that she was diagnosed with the superoxide dismutase 1 (SOD1) gene and amyotrophic lateral sclerosis (ALS).
Raziel Green, 52, an active runner and mother of two, was diagnosed with a rare form of ALS in 2017. Since starting a ...
Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders. Now it’s on the cusp of its first regulatory approval. Each year ...
Tau silencing gene therapy VY1706 robustly reduced tau mRNA levels, with broad distribution, and was well-tolerated in NHP study; IND filing ...
Health Canada confirms it has granted conditional approval to Qalsody to treat adults with ALS in cases linked to a mutation in the superoxide dismutase 1 (SOD1) gene. Paula Trefiak's grandmother ...
Health Canada confirms it has granted conditional approval to Qalsody to treat adults with ALS in cases linked to a mutation in the superoxide dismutase 1 (SOD1) gene. Paula Trefiak's grandmother, ...
By Gina Kolata Researchers have corrected a disease-causing gene mutation with a single infusion carrying a treatment that precisely targeted the errant gene. This was the first time a mutated ...
Copyright 2025 The Associated Press. All Rights Reserved. Actor Gene Hackman arrives with his wife, Betsy Arakawa, for the 60th Annual Golden Globe Awards in Beverly ...
New Mexico officials have announced the cause of death for actor Gene Hackman and his wife Betsy Arakawa, a week after they were found dead at their home in Santa Fe. Hackman died of heart disease ...
Ms. Arakawa, the wife of the actor Gene Hackman, died from the effects of a disease often caused by contact with droppings from infected rodents. By Hank Sanders and Michael Levenson Betsy Arakawa ...