We have now learned why wounds in our mouth don't scar, which could lead to treatments that prevent such blemishes on the ...

This is the first time such results have been achieved in both children and adult patients born with a specific type of ...

Gene therapy has been effective for young children with genetic hearing loss, but this is the first study to show promising ...

A rare case of Epstein-Barr virus-induced Bell palsy in an 18-year-old highlights the need for EBV testing in sudden facial ...

What can a tiny wasp with a rather gruesome parasitic life cycle teach us about evolution, behavior and human developmental ...

Gene expression, where cells use the genetic information encoded in DNA to produce proteins, has been thought of as a dimmer light.

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

In 2024, the FDA approved the first AAV-based gene therapy for DMD, delandistrogene moxeparvovec (Elevidys; Sarepta Therapeutics), in patients aged 4 to 5 years, with the approval subsequently ...

Climate Solutions A gene could be key to growing rice, and feeding billions, in a hotter world Researchers say they can improve rice harvests and grain quality by essentially turning off a ...

CAST systems aren’t found in humans, and when used in human cell cultures they produce a successful DNA insertion only 0.1% of the time—far too low for gene therapy purposes. But after ...